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Table 7 Clinical trials of gilteritinib for AML therapy

From: FLT3 inhibitors in acute myeloid leukemia

Study agents

Disease

Dose

No Pts

Clinical trials

Response

Reference

Gilteritinib

Relapsed

Refractory

20–450 mg/day

252

Phase 1/2

ORR 40%

ORR(FLT+) 52%

[70]

Gilteritinib

Relapsed

Refractory

20–300 mg/day

24

Phase 1

ORR(FLT3+) 80%

ORR(FLT/WT+) 36.4%

[71]

  1. ORR overall response rate